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Current Members

NORD is grateful to the following companies who are active members of the Corporate Council

Pre-Clinical Research Member

Beam Therapeutics

Cabaletta Bio

gMendel

Jaguar Gene Therapy

Neurogene

Orna Therapeutics, Inc

Praxis Precision Medicine

Shape Therapeutics

StrideBio

Tenaya Therapeutics

Vigil Neurosciences

Clinical Development Member

Acer Therapeutics

Aeglea BioTherapeutics

Applied Therapeutics

Arcturus Therapeutics

Asklepion Pharmaceuticals, LLC

Atara Biotherapeutics

Avadel Pharmaceuticals

AVROBIO

bluebirdbio

Camurus

CRISPR Therapeutics

Cytokinetics, Inc.

Dicerna

Editas Medicine

Fulcrum Therapeutics

Insmed Incorporated

Kezar Life Sciences, Inc.

Larimar Therapeutics

Lysogene

MeiraGTx

Mereo BioPharma

Moderna Therapeutics

Orchard Therapeutics Ltd.

Ovid Therapeautics

Passage Bio

Prevail Therapeutics

Prothena

Rallybio

Recursion

REGENXBIO

Rocket Pharmaceuticals, Inc

Sangamo Therapeutics

Saniona

Santen

Savara

Sigilon Therapeutics

Soligenix, Inc.

SpringWorks Therapeutics

Synlogic

uniQure

Wave Life Sciences

X4 Pharmaceuticals

Zealand Pharma

Approved Product Member

AbbVie Pharmaceuticals

Acadia Pharmaceuticals

Agios Pharmaceuticals

Albireo Pharma

Alexion, AstraZeneca Rare Disease

Alnylam Pharmaceuticals

Amgen

Amicus Therapeutics, Inc.

Amryt Pharma

Apellis Pharmaceuticals

argenx

Ascendis Pharma

Astellas

BioCryst

Biogen

BioMarin Pharmaceuticals, Inc.

Blueprint Medicines

Boehringer-Ingelheim Pharmaceuticals

BridgeBio

Bristol-Myers-Squibb

Catalyst Pharmaceuticals

ChemoCentryx

Chiesi Rare Diseases

CSL Behring

Daiichi Sankyo

Deciphera

Dompé

Eiger BioPharmaceuticals

Eli Lilly & Company

Enzyvant

Foundation Medicine

Galderma

Genentech, Inc.

GlaxoSmithKline PLC

Global Blood Therapeutics, Inc.

Greenwich Biosciences, Inc

Harmony Biosciences, LLC

Horizon Therapeutics

Incyte Corporation

Ionis Pharmaceuticals

Ipsen

Janssen Pharmaceuticals

Kiniksa

Kyowa Kirin North America

Mallinckrodt Pharmaceuticals

Neurocrine Biosciences

Novartis

Otsuka America Pharmaceutical, Inc.

Pfizer, Inc.

PharmaEssentia

Pharming Healthcare

PTC Therapeutics

Recordati Rare Diseases

Regeneron

Rigel Pharmaceuticals

Sanofi

Sarepta Therapeutics

Sobi

Spark Therapeutics

Strongbridge Biopharma

Takeda Oncology

Travere Therapeutics, Inc.

UCB Pharma

Vanda Pharmaceuticals Inc.

Vertex Pharmaceuticals Worldwide

Zogenix, Inc.

Business Member

AnovoRX

Biotechnology Industry Organization (BIO)

Eversana

HPS Group LLC.

ICON

Illumina

Medidata

Optum Frontier Therapies

Parexel

PhRMA

Syneos Health