NORD is grateful to the following companies who are active members of the Corporate Council
Beam Therapeutics
Cabaletta Bio
gMendel
Jaguar Gene Therapy
Neurogene
Orna Therapeutics, Inc
Praxis Precision Medicine
Shape Therapeutics
StrideBio
Tenaya Therapeutics
Vigil Neurosciences
Acer Therapeutics
Aeglea BioTherapeutics
Applied Therapeutics
Arcturus Therapeutics
Asklepion Pharmaceuticals, LLC
Atara Biotherapeutics
Avadel Pharmaceuticals
AVROBIO
bluebirdbio
Camurus
CRISPR Therapeutics
Cytokinetics, Inc.
Dicerna
Editas Medicine
Fulcrum Therapeutics
Insmed Incorporated
Kezar Life Sciences, Inc.
Larimar Therapeutics
Lysogene
MeiraGTx
Mereo BioPharma
Moderna Therapeutics
Orchard Therapeutics Ltd.
Ovid Therapeautics
Passage Bio
Prevail Therapeutics
Prothena
Rallybio
Recursion
REGENXBIO
Rocket Pharmaceuticals, Inc
Sangamo Therapeutics
Saniona
Santen
Savara
Sigilon Therapeutics
Soligenix, Inc.
SpringWorks Therapeutics
Synlogic
uniQure
Wave Life Sciences
X4 Pharmaceuticals
Zealand Pharma
AbbVie Pharmaceuticals
Acadia Pharmaceuticals
Agios Pharmaceuticals
Albireo Pharma
Alexion, AstraZeneca Rare Disease
Alnylam Pharmaceuticals
Amgen
Amicus Therapeutics, Inc.
Amryt Pharma
Apellis Pharmaceuticals
argenx
Ascendis Pharma
Astellas
BioCryst
Biogen
BioMarin Pharmaceuticals, Inc.
Blueprint Medicines
Boehringer-Ingelheim Pharmaceuticals
BridgeBio
Bristol-Myers-Squibb
Catalyst Pharmaceuticals
ChemoCentryx
Chiesi Rare Diseases
CSL Behring
Daiichi Sankyo
Deciphera
Dompé
Eiger BioPharmaceuticals
Eli Lilly & Company
Enzyvant
Foundation Medicine
Galderma
Genentech, Inc.
GlaxoSmithKline PLC
Global Blood Therapeutics, Inc.
Greenwich Biosciences, Inc
Harmony Biosciences, LLC
Horizon Therapeutics
Incyte Corporation
Ionis Pharmaceuticals
Ipsen
Janssen Pharmaceuticals
Kiniksa
Kyowa Kirin North America
Mallinckrodt Pharmaceuticals
Neurocrine Biosciences
Novartis
Otsuka America Pharmaceutical, Inc.
Pfizer, Inc.
PharmaEssentia
Pharming Healthcare
PTC Therapeutics
Recordati Rare Diseases
Regeneron
Rigel Pharmaceuticals
Sanofi
Sarepta Therapeutics
Sobi
Spark Therapeutics
Strongbridge Biopharma
Takeda Oncology
Travere Therapeutics, Inc.
UCB Pharma
Vanda Pharmaceuticals Inc.
Vertex Pharmaceuticals Worldwide
Zogenix, Inc.
AnovoRX
Biotechnology Industry Organization (BIO)
Eversana
HPS Group LLC.
ICON
Illumina
Medidata
Optum Frontier Therapies
Parexel
PhRMA
Syneos Health